A Phase I/II Study of BMN053 in Subjects With Duchenne Muscular Dystrophy (DMD)

A Prospective Natural History Study of Progression of Subjects With Duchenne Muscular Dystrophy.

Open Label, Extension Study of PRO044 in Duchenne Muscular Dystrophy (DMD)

Phase IIb Study of PRO045 in Subjects With Duchenne Muscular Dystrophy

Extension Study of BMN 044 in Duchenne Muscular Dystrophy (DMD)

Phase I/II Study of PRO044 in Duchenne Muscular Dystrophy (DMD)

A Phase 1/2 Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of BMN 351 in Participants with Duchenne Muscular Dystrophy