NCT06280209
Trial Status Active Not Recruiting
Duchenne muscular dystrophy (DMD) is a progressive neuromuscular condition caused by a deficiency in dystrophin, an essential protein in muscle fibers. It mostly affects boys, with onset of symptoms around 2 to 3 years of age.
Learn more about our active Duchenne muscular dystrophy clinical trials below. To view all BioMarin’s historical trials in Duchenne muscular dystrophy, click here.
NCT06280209
Trial Status Active Not Recruiting
