Duchenne muscular dystrophy (DMD) is a progressive neuromuscular condition caused by a deficiency in dystrophin, an essential protein in muscle fibers. It mostly affects boys, with onset of symptoms around 2 to 3 years of age.

Learn more about our active Duchenne muscular dystrophy clinical trials below. To view all BioMarin’s historical trials in Duchenne muscular dystrophy, click here.