BioMarin Clinical Trials logo
  • Guide to Clinical Trials
    • Understanding Clinical Trials
    • Our Commitment
    • FAQs
  • Areas of Clinical Research
    • Achondroplasia
    • Alpha-1 Antitrypsin Deficiency
    • Duchenne Muscular Dystrophy
    • Hypochondroplasia
    • Idiopathic Short Stature
    • Noonan Syndrome
    • Phenylketonuria
    • SHOX Deficiency
    • Turner Syndrome
  • HCP
  • BioMarin.com
Contact
  • Contact

SHOX Deficiency

SHOX deficiency, or short stature homeobox-containing gene deficiency, is a genetic condition caused by changes to or absence of the SHOX gene. SHOX deficiency is associated with a wide spectrum of short-stature phenotypes, including Turner syndrome and Léri–Weill dyschondrosteosis.

Learn about our active SHOX deficiency clinical trials below.

SHOX Deficiency Clinical Trials

NCT06668805

Trial Status Recruiting

A Phase 2 Basket Study of Vosoritide in Children With Turner Syndrome, SHOX Deficiency and Noonan Syndrome With an Inadequate Response to Human Growth Hormone

Learn More

Print

Understanding Clinical Trials

Mother and child sit opposite a doctor at a desk

Our Commitment

Miranda Newquist in San Rafael Lab

Frequently Asked Questions

HCP filling out paperwork

You're leaving the BioMarin Clinical Trials website.

This will take you to BioMarin.com, our global corporate website. Some of the information on BioMarin.com is intended for U.S. audiences only.

Leave this website Close

You’re leaving the BioMarin Clinical Trials website.

Links to sites outside of this website are provided as a resource to the viewer. BioMarin accepts no responsibility for the content of linked sites.

Leave this website Close

BioMarin Clinical Trials logo
  • Privacy Policy
  • Terms of Use
  • Supply Chain Statement
  • Report an Adverse Event
  • Cookie Settings
  • LinkedIn
  • X
  • Instagram
  • Facebook

© 2025 BioMarin. All rights reserved. MMRC-MPRL-00150 03/25