A Study to Assess Growth in Children With Idiopathic Short Stature

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Trial Status Recruiting

Trial Identifier

NCT06309979

Condition

Idiopathic Short Stature

The below information is taken directly from public registry websites such as ClinicalTrials.gov, EuClinicalTrials.eu, ISRCTN.com, etc. and has not been edited.

Trial Summary

Study 111-903 will generate baseline growth data in children with ISS by collecting growth measurements and other variables of interest.

Eligibility Criteria

Birth Sex

All

Age

2 Years to 16 Years

Healthy Volunteers

No

Study Type:

Observational

Number of Participants:

300

Study Started:

2024-08-08

Study Updated:

2025-04-17

Trial Locations

  • Harbor-UCLA Medical Center - The Lundquist Institute (Los Angeles Biomedical Research Institute (LA BioMed)

    Los Angeles, California, United States

  • Center Of Excellence in Diabetes and Endocrinology

    Sacramento, California, United States

  • University of California San Francisco (UCSF)

    San Francisco, California, United States

  • Children's National Health System

    Washington, District of Columbia, United States

  • Nemours Children's Clinic

    Jacksonville, Florida, United States

  • Nicklaus Children's Hospital

    Miami, Florida, United States

  • Nemours Children's Health System - Corporate Headquarters

    Pensacola, Florida, United States

  • Centricity Research

    Columbus, Georgia, United States

  • St. Luke's Children's Endocrinology

    Boise, Idaho, United States

  • Rocky Mountain Clinical Research - Idaho Falls

    Idaho Falls, Idaho, United States

  • University of Louisville School Of Medicine - Norton Children's Hospital

    Louisville, Kentucky, United States

  • University of Minnesota Medical School - Masonic Children's Hospital - Pediatric Specialty Care Explorer Clinic

    Minneapolis, Minnesota, United States

  • Montefiore Medical Center (MMC) - The Children's Hospital at Montefiore (CHAM)

    Bronx, New York, United States

  • UBMD Pediatrics

    Buffalo, New York, United States

  • ACGC Research, NYU Ambulatory Care Garden City

    Garden City, New York, United States

  • Icahn School of Medicine at Mount Sinai (ISMMS) - The Mount Sinai Hospital (MSH) - Pediatric Associates

    New York, New York, United States

  • Cincinnati Children's Hospital Medical Center Burnet Campus

    Cincinatti, Ohio, United States

  • Cook Children's Endocrinology

    Fort Worth, Texas, United States

  • Charleston Area Medical Center (CAMC) Health System

    Charleston, West Virginia, United States

Inclusion Criteria

1. Participants must be > 2 years old, and ≤ 14 years old (female) or ≤ 16 years old (males) at the time of signing the informed consent.
2. A height assessment corresponding to a height Z-score of ≤ -2.25 SDs in reference to the general population of the same age and sex, as calculated using the Centers for Disease Control and Prevention (CDC) growth chart (https://www.cdc.gov/growthcharts/zscore.htm).
3. Participants who have either never received hGH, or who are currently receiving hGH treatment.
4. Historic stimulation test result with serum or plasma GH level greater than 10 μg/L.
5. Parent(s) or guardian(s) are willing and able to provide written, signed informed consent.

Exclusion Criteria

1. Diagnosis of systemic disease or condition that may cause short stature, eg renal, neoplastic, pulmonary, cardiac, gastrointestinal, immunologic and metabolic disease. Children with such diagnoses can be considered for inclusion if their condition is well controlled, at the discretion of the Medical Monitor.
2. Known presence of one or more pituitary hormone deficiencies
3. Bone age advanced over chronological age by more than 3 years.
4. For hGH naïve participants, historic stimulation test result with serum or plasma GH level greater than 10 μg/L or serum IGF-1 in the normal range for age (between -1.00 SDs and +2.00 SDs).
5. For participants currently on hGH treatment, historic results before GH treatment of stimulation test with serum or plasma GH level greater than 10 μg/L or serum IGF-1 test between -1.00 SDs and +2.00 SDs.
6. Have received an investigational product (IP) or investigational medical device for any purpose within 6 months before the Screening visit.

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