A Prospective Study Evaluating Seroprevalence and Seroconversion of Antibodies Against Adeno-associated Virus (AAV)

Interested in this Trial?

Contact Us

Trial Status Terminated

Trial Identifier

NCT05580692

Condition

Hemophilia A, Hemophilia a

The below information is taken directly from public registry websites such as ClinicalTrials.gov, EuClinicalTrials.eu, ISRCTN.com, etc. and has not been edited.

Trial Summary

A prospective cohort study utilizing biospecimen sample collection from adult Hemophilia A subjects to evaluate and characterize seroprevalence and the seroconversion of antibodies against AAV serotypes

Eligibility Criteria

Birth Sex

All

Age

From 18 Years

Healthy Volunteers

No

Drug/Treatment:

Biospecimen Collection

Phase:

Na

Study Type:

Interventional

Number of Participants:

321

Study Started:

2023-03-14

Study Updated:

2024-08-19

Trial Locations

  • Instituto Hematologia Arbesu

    Godoy Cruz, Mendoza, Argentina

  • Hospital Ramon Jose Vidal

    Corrientes, , Argentina

  • Medico Hematologo

    Mendoza, , Argentina

  • Instituto de Hematologia y Medicina Clinica Dr. RUben Davoli

    Rosario, , Argentina

  • Royal Prince Alfred Hospital

    Camperdown, , Australia

  • Haemophilia and Haemostasis Centre Level 1 Cancer Centre South Metropolitan Health Service Fiona Stanley Hospital

    Murdoch, , Australia

  • Medical University of Vienna

    Wien, , Austria

  • King Faisal Specialist Hospital & Research Center

    Riyadh, , Saudi Arabia

  • King Saud University Medical City King Saud University

    Riyadh, , Saudi Arabia

  • Skane University Hospital

    Malmö, , Sweden

  • ME Centrum för kliniska cancerstudier - House H3

    Solna, , Sweden

  • Acibadem Adana Hospital

    Adana, , Turkey

  • Hacettepe University

    Ankara, , Turkey

  • Gaziantep University Medical Faculty Sahinbey Educational Research Hospital

    Gaziantep, , Turkey

  • Istanbul University Cerrahpasa - Cerrahpasa Medical Faculty

    Istanbul, , Turkey

  • Ege University Medical Faculty

    İzmir, , Turkey

  • Ondokuz Mayis Univ. Med. Fac.

    Samsun, , Turkey

  • Sheikh Shakhbout Medical City

    Abu Dhabi, , United Arab Emirates

Inclusion Criteria

  • Adult Subjects with Hemophilia A

Exclusion Criteria

  • Subject previously treated with AAV vector gene therap

Contact BioMarin Clinical Trials

Please complete and submit the following form to express interest in participating and request more information about one of our clinical trials.

By completing this form and clicking the send button, you understand and hereby consent to storage of your personal information, including within the United States and Europe, which will be accessible by BioMarin for purposes such as responding to your request, quality control, fulfilling compliance obligations, and assisting with products, services, or clinical trials. Depending on where you live, you may have the right to request access to, removal, or correction of your personal information held by BioMarin. You may submit your request via the contact information and/or webform located within the full BioMarin Privacy Policy.

*required fields

"*" indicates required fields

This field is hidden when viewing the form
This field is hidden when viewing the form