NCT02191917
Late-onset Pompe Disease
The below information is taken directly from public registry websites such as ClinicalTrials.gov, EuClinicalTrials.eu, ISRCTN.com, etc. and has not been edited.
Study 701-201 is a study in patients with late-onset Pompe disease (LOPD). The study will test respiratory muscle strength initially and again after 24 weeks in subjects treated or not treated with BMN 701 .
All
From 18 Years
No
Respiratory muscle strength measurements by different techniques.
Observational
8
2014-10-21
2023-01-09
Gainesville, Florida, United States
London, , United Kingdom
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