NCT00104247
Phenylketonuria, Phenylketonurias
The below information is taken directly from public registry websites such as ClinicalTrials.gov, EuClinicalTrials.eu, ISRCTN.com, etc. and has not been edited.
The primary objective of this study is to evaluate the efficacy of Phenoptin™ (sapropterin dihydrochloride) in reducing blood phenylalanine (Phe) levels in subjects with phenylketonuria.
All
From 8 Years
No
sapropterin dihydrochloride, 6R-BH4, tetrahydrobiopterin
Phase 3
Interventional
89
2005-03
2014-07-23
Los Angeles, California, United States
Oakland, California, United States
New Haven, Connecticut, United States
Chicago, Illinois, United States
Boston, Massachusetts, United States
Minneapolis, Minnesota, United States
St. Louis, Missouri, United States
New York, New York, United States
Portland, Oregon, United States
Pittsburgh, Pennsylvania, United States
Dallas, Texas, United States
Salt Lake City, Utah, United States
Madison, Wisconsin, United States
*required fields
"*" indicates required fields